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The treatment of juvenile/adult GM1-gangliosidosis with Miglustat may reverse disease progression

Federica Deodato; Elena Procopio; Angelica Rampazzo; Roberta Taurisano; Maria Alice Donati; Carlo Dionisi-Vici; Anna Caciotti; Amelia Morrone; Maurizio Scarpa
Metabolic Brain Disease · Vol. 32, Issue 5 · pp. 1529-1536 · 2017

Abstract

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Bibliographic Information

JournalMetabolic Brain Disease
PublisherSpringer
Publication Date2017-10-01
Publication Year2017
Volume32
Issue5
Pages1529-1536
Document TypeJournal Article
eISSN1573-7365
DOI10.1007/s11011-017-0044-y

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NARA Access Coverage1986-01-01~Current
Journal Homepagehttps://www.springer.com/journal/11011
Publisher PageOpen Publisher Page
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