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Preclinical Evaluation of AAV8-R338L Gene Therapy for Hemophilia: Efficacy, Pharmacokinetics, Distribution, Excretion and Toxicity in Mouse Models and Non-human Primates

Dehu Dou; Jing Lu; Deli Li; Fengxia He; Xi Zhu; Xuefeng Zhang; Xijing Chen
Pharmaceutical Research · Vol. 42, Issue 10 · pp. 1717-1732 · 2025

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Bibliographic Information

JournalPharmaceutical Research
PublisherSpringer
Publication Date2025-10-01
Publication Year2025
Volume42
Issue10
Pages1717-1732
Document TypeJournal Article
Print ISSN0724-8741
eISSN1573-904X
DOI10.1007/s11095-025-03918-z

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NARA Access Coverage1984-01-01~Current
Journal Homepagehttps://www.springer.com/journal/11095
Publisher PageOpen Publisher Page
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