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Lipid nanoparticle-mediated base-editing of the Hao1 gene achieves sustainable primary hyperoxaluria type 1 therapy in rats

Dexin Zhang; Rui Zheng; Zhoutong Chen; Liren Wang; Xi Chen; Lei Yang; Yanan Huo; Shuming Yin; Dan Zhang; Jiaxin Huang; Xingang Cui; Dali Li; Hongquan Geng
Science China Life Sciences · Vol. 67, Issue 12 · pp. 2575-2586 · 2024

Abstract

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Bibliographic Information

JournalScience China Life Sciences
PublisherSpringer
Publication Date2024-12-01
Publication Year2024
Volume67
Issue12
Pages2575-2586
Document TypeJournal Article
Print ISSN1674-7305
eISSN1869-1889
DOI10.1007/s11427-024-2697-3

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NARA Access Coverage1997-01-01~Current
Journal Homepagehttps://www.springer.com/journal/11427
Publisher PageOpen Publisher Page
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