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CRISPR/Cas9-mediated promoterless gene targeting reduces lysosome storage in MPS VII mice

Linlin Shan; Qiongyan He; Weifeng Zhang; Xiaojing Zheng; Junli Zhao; Peiyan Yang; Qinwen Mao; Haibin Xia
Science China Life Sciences · Vol. 68, Issue 9 · pp. 2697-2706 · 2025

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Bibliographic Information

JournalScience China Life Sciences
PublisherSpringer
Publication Date2025-09-01
Publication Year2025
Volume68
Issue9
Pages2697-2706
Document TypeJournal Article
Print ISSN1674-7305
eISSN1869-1889
DOI10.1007/s11427-024-2915-x

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NARA Access Coverage1997-01-01~Current
Journal Homepagehttps://www.springer.com/journal/11427
Publisher PageOpen Publisher Page
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