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Journal Article

Model-Informed Approach Supporting Approval of Nexviazyme (Avalglucosidase Alfa-ngpt) in Pediatric Patients with Late-Onset Pompe Disease

Ruo-Jing Li; Lian Ma; Katarzyna Drozda; Jie Wang; Ann R. Punnoose; Linda J. B. Jeng; Janet W. Maynard; Hao Zhu; Michael Pacanowski
The AAPS Journal · Vol. 25, Issue 1 · 2023

Abstract

Abstract is unavailable.

Bibliographic Information

JournalThe AAPS Journal
PublisherSpringer
Publication Date2023-01-18
Publication Year2023
Volume25
Issue1
Document TypeJournal Article
eISSN1550-7416
DOI10.1208/s12248-023-00784-8

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NARA Access Coverage1999-01-01~Current
Journal Homepagehttps://www.springer.com/journal/12248
Publisher PageOpen Publisher Page
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