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Best Practices for Development and Validation of Enzymatic Activity Assays to Support Drug Development for Inborn Errors of Metabolism and Biomarker Assessment

Mitra Azadeh; Jeremy Good; Michele Gunsior; Nadia Kulagina; Yanmei Lu; Jim McNally; Heather Myler; Yan G. Ni; Ryan Pelto; Karen J. Quadrini; Catherine Vrentas; Lin Yang
The AAPS Journal · Vol. 26, Issue 5 · 2024

Abstract

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Bibliographic Information

JournalThe AAPS Journal
PublisherSpringer
Publication Date2024-08-23
Publication Year2024
Volume26
Issue5
Document TypeJournal Article
eISSN1550-7416
DOI10.1208/s12248-024-00966-y

Access Information

NARA Access Coverage1999-01-01~Current
Journal Homepagehttps://www.springer.com/journal/12248
Publisher PageOpen Publisher Page
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